The purpose of this study is to evaluate the safety, tolerability and pharmacokinetics (PK)
of 5 escalating doses of SRP-5051 administered as a single dose to patients with DMD amenable
to exon 51 skipping treatment.
The purpose of this study is to learn if group-based phone counseling is effective for
increasing breastfeeding rates, reducing the early introduction of solids and increasing
maternal weight loss after pregnancy.
The primary purpose of this project is to determine if acute monitoring of shunt patency via
ultrasound elastography measurements of splenic stiffness before and after TIPS placement
results in reduced morbidity and mortality from shunt failure.